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RPE65-associated Leber congenital amaurosis

Showing 1 - 25 of >10,000
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Leber Congenital Amaurosis Trial (HG004)

Not yet recruiting
  • Leber Congenital Amaurosis
  • (no location specified)
Jun 13, 2023

Leber Congenital Amaurosis Associated With Mutations in RPE65

Recruiting
  • Leber Congenital Amaurosis
    • Ann Arbor, Michigan
    • +1 more
    Apr 7, 2022

    Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia

    Active, not recruiting
    Has Results
    • Inherited Retinal Dystrophy Due to RPE65 Mutations
    • Leber Congenital Amaurosis
    • AAV2-hRPE65v2,voretigene neparvovec-rzyl
    • Iowa City, Iowa
    • +1 more
    Dec 9, 2021

    Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)

    Active, not recruiting
    • Amaurosis of Leber
    • Retinal Diseases
    • rAAV2-CBSB-hRPE65
    • Gainesville, Florida
    • +1 more
    Dec 13, 2021

    Leber Congenital Amaurosis Trial in Ann Arbor, London (AAV RPE65)

    Completed
    Has Results
    • Leber Congenital Amaurosis
    • AAV RPE65
    • Ann Arbor, Michigan
    • +1 more
    Jun 17, 2021

    To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)

    Not yet recruiting
    • To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
    • (no location specified)
    Aug 29, 2023

    Leber Congenital Amaurosis Trial in Shanghai (HG004)

    Recruiting
    • Leber Congenital Amaurosis
    • HG004
    • Shanghai, Shanghai, China
      Xinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
    Oct 12, 2023

    Leber Congenital Amaurosis Trial in Shanghai (HG004)

    Recruiting
    • Leber Congenital Amaurosis
    • HG004
    • Shanghai, Shanghai, China
      Xinhua Hospital affiliated with Shanghai Jiao Tong University Sc
    Sep 26, 2023

    Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)

    Completed
    • Leber Congenital Amaurosis
    • voretigene neparvovec-rzyl
    • Philadelphia, Pennsylvania
      The Children's Hospital of Philadelphia
    Oct 30, 2020

    Choroideremia Trial in Edmonton (rAAV2.REP1 vector)

    Completed
    • Choroideremia
    • rAAV2.REP1 vector
    • Edmonton, Alberta, Canada
      University of Alberta
    May 16, 2022

    Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in United States (AAV2-hRPE65v2,voretigene

    Active, not recruiting
    • Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
    • AAV2-hRPE65v2,voretigene neparvovec-rzyl
    • Los Angeles, California
    • +9 more
    Oct 22, 2021

    Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

    Active, not recruiting
    • Inherited Retinal Dystrophy Due to RPE65 Mutations
    • AAV2-hRPE65v2
    • (no location specified)
    Dec 9, 2021

    Leber Congenital Amaurosis Trial in Jerusalem (rAAV2-hRPE65)

    Completed
    • Leber Congenital Amaurosis
    • rAAV2-hRPE65
    • Jerusalem, Israel
      Hadassah Medical Organization
    Apr 8, 2018

    Leber Hereditary Optic Neuropathy Trial in Wuhan (rAAV2-ND4)

    Active, not recruiting
    • Leber Hereditary Optic Neuropathy
    • Wuhan, Hubei, China
      Department of Ophthalmology，Tongji Hospital, Tongji Medical Coll
    Sep 15, 2020

    Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney

    Recruiting
    • Rare Disorders
    • +309 more
      • Sioux Falls, South Dakota
      • +1 more
      Jun 20, 2022

      Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in Beijing (FT-001 Low Dose, FT-001 Mid Dose, FT-001 High Dose)

      Recruiting
      • Biallelic RPE65 Mutation-associated Retinal Dystrophy
      • FT-001 Low Dose
      • +2 more
      • Beijing, Beijing, China
        Peking Union Medical College Hospital
      May 11, 2023

      Leber Congenital Amaurosis Trial in Worcester, Portland (rAAV2-CB-hRPE65)

      Completed
      Has Results
      • Leber Congenital Amaurosis
      • rAAV2-CB-hRPE65
      • Worcester, Massachusetts
      • +1 more
      Dec 1, 2017

      Leber Congenital Amaurosis 10, Inherited Retinal Dystrophies, Eye Diseases, Hereditary Trial in United States (EDIT-101)

      Active, not recruiting
      • Leber Congenital Amaurosis 10
      • +6 more
      • Miami, Florida
      • +4 more
      Dec 2, 2022

      Acute LHON, Onset Within Three Months, Onset Between 3 to 6 Months Trial in Wuhan (rAAV2-ND4)

      Unknown status
      • Acute LHON
      • +6 more
      • Wuhan, Hubei, China
        Department of Ophthalmology ，Tongji Hospital, Tongji Medical Col
      Jul 27, 2020

      Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen, Sham)

      Active, not recruiting
      • Leber Congenital Amaurosis 10
      • +9 more
      • Iowa City, Iowa
      • +13 more
      Mar 2, 2022

      Cell Collection to Study Eye Diseases

      Recruiting
      • Retinal Disease
      • +3 more
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Jan 23, 2023

        Retinal Disorder Trial in New York (Placebos, ZA Low dose, ZA high dose)

        Suspended
        • Retinal Disorder
        • Placebos
        • +2 more
        • New York, New York
          NY NY
        Oct 7, 2020

        Leber Congenital Amaurosis, Retinitis Pigmentosa Trial in Beijing (Human primary Retinal Pigment Epithelial (HuRPE) cells)

        Unknown status
        • Leber Congenital Amaurosis, Retinitis Pigmentosa
        • Human primary Retinal Pigment Epithelial (HuRPE) cells
        • Beijing, China
          Beijing Tongren Hospital
        Aug 7, 2018

        Retinitis Pigmentosa Trial in Bangkoknoi (BM-MSC)

        Completed
        • Retinitis Pigmentosa
        • BM-MSC
        • Bangkoknoi, Bangkok, Thailand
          Siriraj Hospital Mahidol University
        Aug 31, 2021

        Genetic Variants in Nicotinamide Adenine Dinucleotide Synthesis

        Active, not recruiting
        • Vacterl Association
        • Congenital Malformation
          • Rochester, Minnesota
            Mayo Clinic
          Jan 10, 2023